Course Information
Description
In recent years, close collaboration between multiple scientific disciplines has rendered gene therapy a viable treatment option for some genetic conditions, and a promising pursuit for many others. As of today, there are numerous clinical trials underway for gene therapy treatments of various cancers, blood disorders, neurological diseases, and inherited retinal disorders to name a few. Advancements in vector science, gene editing technologies, and our understanding of the molecular underpinnings of disease continue to pave the way for the development of additional gene therapy treatments aimed at improving patient quality of life and prolonging lifespan. As this field continues to expand, so too will the number of genetic conditions that can be treated and possibly even cured with gene therapy, making this an exciting time to delve into this field.
This advanced course offers a unique way for professionals to learn from leading Harvard Medical School faculty about gene therapy and about the advances happening in this field that are ultimately helping to improve the treatment of certain genetic diseases.
This is a fully online course. Students registering for this course will be automatically enrolled by HMX and will receive a confirmation email from onlinelearning@hms.harvard.edu three days prior to the HMX course start date. All course-related activities will happen through the HMX online platform. Students who complete the course will receive a Certificate of Completion. For more information please see the FAQ on the HMX website
https://learn.hms.harvard.edu/frequently-asked-questions and then click on the HMX ONLINE LEARNING link; register via my.harvard, do not use the “apply now” buttons on the HMX website.
Class Notes
Students must enroll in this course no later than September 8, 2026.
This course is intended for master's students only. Students must complete this course between September 8 and November 20, 2026.
Not Available for Cross Registration